Rare diseases: a race against time and systemic barriers

13 March 2025 • 15:00 -16:00 • conference room 24

Online broadcast session

  • Challenges in diagnosing rare diseases
  • Difficulties in accessing therapies for rare diseases
  • Early diagnosis as key to effective treatment
  • Overview of available medicines and gene therapies for rare diseases
  • The role of clinical trials and international collaboration in the treatment of rare diseases
Back